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n-Lorem Foundation Partners with Ultragenyx to Bolster Development of Personalized Medicines for Patients with Ultra-Rare Diseases americanpharmaceuticalreview
April 07, 2021
n-Lorem Foundation announced a new partnership with Ultragenyx Pharmaceutical, a biopharmaceutical company focused on the development and commercialization of novel products for serious rare and ultra-rare genetic diseases.
New NICE ultra-rare disease proposals "not fit for purpose", says BIA pharmafile
January 17, 2017
The BioIndustry Association (BIA) has accused new proposals put forward by the National Institute for Health and Care Excellence (NICE) of being “not fit for purpose” and potentially denying patients from accessing treatments for ultra-rare disease.