US-based biotechnology company Casma Therapeutics has secured $50m in a Series B financing round to support the development of a programme targeting muscular dystrophy treatment.
Pfizer Inc. (NYSE: PFE) announced that it is terminating two ongoing clinical studies evaluating domagrozumab (PF-06252616) for the treatment of Duchenne muscular dystrophy (DMD): a Phase 2 safety and efficacy study (B5161002) and an open-label extension
For the first time, scientists report using gene-editing technology to halt the progression of muscular dystrophy in dogs -- suggesting a possible breakthrough for children with a form of the disease.
Sarepta is determined to stay at the forefront of genetic medicines for muscular dystrophies and to that end has signed another R&D deal—this time with Myonexus Therapeutics—and taken an option on buying the company.
Long-term treatment with selective estrogen receptor modulators improves muscle, respiratory, and skeletal function without weakening bone in new mouse studies…