The UK’s National Institute for Health and Clinical Excellence (NICE) has recommended the use of subcutaneous injection of Takeda’s Takhzyro (lanadelumab) to prevent recurrent attacks ...
Santhera Pharmaceuticals has licensed a drug called Raxone, indicated for the treatment of Leber’s hereditary optic neuropathy (LHON), to Chiesi Farmaceutici (Chiesi Group).
New study found that both genetic and epigenetic differences between the maternal and paternal allele contributed to the observed tissue-specific activity patterns, uncovering the first complete allelome.