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CRISPR, Capsida team up on gene-edited therapies for ALS, Friedreich's ataxia
June 16, 2021CRISPR Therapeutics has inked a partnership with newly launched Capsida Biotherapeutics to develop and commercialise in vivo gene-editing therapies delivered with engineered adeno-associated virus (AAV) vectors for the treatment of familial amyotrophic -
Retrotope Announces First Dosing of RT001 in Friedreich’s Ataxia Study
January 15, 2020Retrotope has dosed its first patient in a Phase 2/3 clinical trial of RT001 in Friedreich’s ataxia, the most common of the inherited ataxias. RT001, a stabilized fatty acid drug, has been shown to reduce lipid peroxidation leading to cell death in ...
Pharma Sources Insight January 2025
