-
Experimental gene therapy reverses sickle cell disease for three years
EuropeanPharmaceuticalReview
December 15, 2021
A study of an investigational gene therapy for sickle cell disease at Columbia University Irving Medical Centre, US, has found that a single dose restored blood cells to their normal shape...
-
Could Gene Therapy Help Cure Sickle Cell Disease?
Drugs
December 14, 2021
A gene therapy that could provide a permanent cure for sickle cell disease continues to show success through a third wave of patients, researchers report.
-
Neurophth Raised Over $60 Million USD in Series-C Financing to Advance Gene Therapies
prnasia
November 24, 2021
Neurophth Therapeutics Ltd., ("Neurophth"), a fully integrated genomic medicines company dedicated on seeking to improve lives through the curative potential of gene therapies...
-
Thermo Fisher Launches Gibco AAV Production System
ContractPharma
November 12, 2021
Thermo Fisher Scientific has launched the integrated Gibco AAV-MAX Helper Free AAV Production System, a complete, optimized solution that aims to simplify the AAV vector production workflow.
-
Forge Biologics to provide CDMO support for Solid Biosciences' preclinical gene therapy
CPhIonline
October 10, 2021
By providing AAV process development, scale up and cGMP manufacturing services, Forge hopes to bolster Solid's gene therapy pipeline
-
Belief Biomed's Gene Therapy for Hemophilia B Receives NMPA IND Approval: First Intravenous Infusion Gene Therapy for Rare Disease in China
prnasia
August 11, 2021
On August 10th, 2021,Belief Biomed announced that China's National Medical Products Administration (NMPA) has cleared the IND (Investigational New Drug) application for Belief Biomed's BBM-H901.
-
Integral Molecular Launches Transgene Protein Engineering Platform to Address Challenges in Gene Therapy
americanpharmaceuticalreview
August 02, 2021
Integral Molecular, the industry leader in membrane proteins, announces the launch of GeneCanvas, its proprietary protein engineering platform to optimize transgenes and other gene therapy elements.
-
Kriya Therapeutics Completes Renovation of Its Facility for Scalable Gene Therapy Manufacturing
firstwordpharma
July 29, 2021
Kriya Therapeutics, Inc. today announced the completion of the renovation of its 51,000 square foot facility located in Research Triangle Park, North Carolina to support cGMP production of its expanding pipeline of gene therapies.
-
AavantiBio, Aldevron Form Gene Therapy Partnership
contractpharma
July 28, 2021
Aldevron will supply plasmids to AavantiBio’s planned vector core and CDMO partners.
-
New targeted gene therapy could reverse neurological diseases
europeanpharmaceuticalreview
July 15, 2021
Researchers have developed a novel gene therapy that could help treat children with incurable genetic and neurodegenerative diseases.