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AHA News: This Faulty Gene May Help Predict Heart Muscle Disease
drugs
June 21, 2019
This Faulty Gene May Help Predict Heart Muscle Disease.
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Axovant, Yposkesi Ink Gene Therapy Pact
contractpharma
June 21, 2019
CDMO to support the global development and commercialization of Axovant’s gene therapy programs.
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Voyager Therapeutics, Sanofi Genzyme Restructure Gene Therapy Alliance
contractpharma
June 18, 2019
Voyager gains worldwide rights to VY-HTT01 Huntington’s disease program and ex-U.S. rights to VY-FXN01 Friedreich’s ataxia program for $10 million upfront.
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Catalent Biologics, IVERIC bio Ink Mfg. Pact
contractpharma
June 18, 2019
Paragon Gene Therapy, part of Catalent Biologics, will provide materials for preclinical and Phase 1/2 trials for IVERIC’s gene therapy product candidates.
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Gene Test Might Someday Gauge Your Heart Attack Risk
drugs
June 12, 2019
Gene Test Might Someday Gauge Your Heart Attack Risk.
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Biogen Completes $800M Nightstar Acquisition
contractpharma
June 10, 2019
Gains two mid- to late-stage clinical assets and preclinical programs in ophthalmology.
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Cleveland researchers test novel gene therapy for glioblastoma
worldpharmanews
June 10, 2019
Cleveland researchers test novel gene therapy for glioblastoma.
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Aldevron to Build 14-Acre Gene Therapy Mfg. Campus
contractpharma
June 04, 2019
Annual capacity will exceed $1 billion of plasmid DNA, RNA, gene editing enzymes, and other biologics.
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Blood Test Could Spot Multiple Cancer Types, Researchers Say
drugs
May 30, 2019
A gene-based blood test can accurately detect breast, colorectal, lung, ovarian, pancreatic, gastric or bile duct cancers in patients, researchers report.
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FDA approves first gene therapy for paediatric spinal muscular atrophy
europeanpharmaceuticalreview
May 30, 2019
The FDA has given approval to AveXis for the first treatment of paediatric spinal muscular atrophy (SMA).