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Cheaper drug just as effective protecting heart in Duchenne muscular dystrophy
worldpharmanews
September 27, 2019
A new clinical trial conducted at The Ohio State University Wexner Medical Center found a cost-effective generic medication works just as well as a more expensive drug in preserving cardiovascular function in boys with ...
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Cumberland Announces FDA Orphan Drug Grant Award for Ifetroban
americanpharmaceuticalreview
September 26, 2019
Cumberland Pharmaceuticals announced FDA Orphan Drug Grant funding for a new Phase II clinical program. The Company has initiated the clinical development of ifetroban for the treatment ...
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Solid tanks as safety scare again rocks DMD gene therapy
fiercebiotech
May 15, 2019
A safety scare has rocked Solid Biosciences’ drive to get its Duchenne muscular dystrophy (DMD) gene therapy program back on track.
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New drug for Duchenne muscular dystrophy clears phase 1 clinical trial
worldpharmanews
February 22, 2019
Patients with Duchenne muscular dystrophy (DMD) have few treatment options.
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Muscle stem cells can drive cancer that arises in Duchenne muscular dystrophy
worldpharmanews
January 16, 2019
People with Duchenne muscular dystrophy (DMD) can develop an otherwise-rare muscle cancer, called rhabdomyosarcoma, due to the muscle cells' continuous work to rebuild the damaged tissue.
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Pfizer ends two Duchenne muscular dystrophy drug trials
pharmatimes
September 14, 2018
Pfizer is shutting down two clinical studies assessing the anti-myostatin monoclonal antibody domagrozumab (PF-06252616) for the treatment of Duchenne muscular dystrophy (DMD).
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Sarepta shares surge after gene therapy leads to microdystrophin expression in DMD patients
pharmafile
June 22, 2018
This week, shares in Sarepta Therapeutics rocketed by 80% after the company released preliminary data from a Phase 1/2a trial showing that its experimental gene therapy
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Sarepta to Seek FDA Approval for Second DMD Treatment
biospace
March 13, 2018
Sarepta Therapeutics (Formerly known as AVI BioPharma, Inc.) is planning on seeking approval of a second treatment for Duchenne muscular dystrophy (DMD).
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Solid Biosciences Discloses DMD Trial Setback Amid $125M IPO Push
biospace
January 29, 2018
Solid Biosciences' failure to disclose some negative issues related to its work on a treatment for Duchenne muscular dystrophy (DMD) not only complicated its upcoming initial public offering (IPO), but is casting some shade on DMD research in general.
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Astellas buys DMD drug in $450M mitochondrial takeover
fiercebiotech
December 04, 2017
Astellas has acquired its partner Mitobridge in a deal worth up to $450 million. The takeover gives Astellas full control of a phase 1 Duchenne muscular dystrophy (DMD) drug in return for $225 million upfront and the same again down the line.